Early Bird Deadline: Register by December 15th, 2025, to take advantage of reduced rates. On-site Registration: Available, ...
HYOGO, Japan--(BUSINESS WIRE)--JCR Pharmaceuticals Co., Ltd. (TSE: 4552) made significant contributions at the Society for the Study of Inborn Errors of Metabolism (SSIEM) Annual Symposium 2024, held ...
Orphan Drug Designation for MPS II builds on Immusoft's clinical progress in MPS I and supports expansion of its engineered B cell platform across multiple indications SAN FRANCISCO, Dec. 15, 2025 ...
NEW DELHI: (Dec 11) The Indian Medical Parliamentarians Forum (IMPF) -- ”a cross-party group of 45 MPs who are also medical professionals -- ”has sought uninterrupted access to Enzyme Replacement ...
HYOGO, Japan--(BUSINESS WIRE)--JCR Pharmaceuticals Co., Ltd. (TSE 4552: Chairman and President Shin Ashida, “JCR”) announced presentations highlighting its latest advancements in gene therapy research ...
The Indian Medical Parliamentarians Forum (IMPF) - a cross-party group of 45 MPs who are also medical professionals -- has sought uninterrupted access to Enzyme Replacement Therapy for children ...
Denali Therapeutics Inc. DNLI recently outlined its roadmap for 2026 across its portfolio of investigational therapies for ...
A Denali treatment for a rare lysosomal storage disorder, Hunter syndrome, has posted encouraging biomarker results in a small, open-label Phase 1/2 trial. The genetic disorder is caused by mutations ...