Changes in motor units closely reflect disease severity in people with spinal muscular atrophy (SMA), suggesting potential ...

British singer Jesy Nelson recently took to Instagram to share a devastating update about her 8-month-old twin daughters.

Intrathecal onasemnogene abeparvovec improved HFMSE scores in patients with SMA type 2, indicating enhanced motor function. The STEER study confirmed the therapy's favorable safety profile, with ...

We were unable to process your request. Please try again later. If you continue to have this issue please contact [email protected]. Topline results from a phase 3 clinical trial showed an ...

The singer shared an emotional update about her twins’ health on Sunday and that ‘time is of the essence with this disease’ ...

"Decreasing AMMO [active maximal mouth opening] over time is seen most often in patients with SMA type 2 with an estimated reduction of almost 1 mm per year...At this point, we propose that ...

Some patients with later-onset spinal muscular atrophy (SMA) type 2 and type 3 had improved motor function when the investigational monoclonal antibody apitegromab was added to their treatment, the ...

SMA Type 1 is a severe genetic disorder affecting muscle strength and mobility. Former Little Mix star Jesy Nelson reveals ...

In a multidisciplinary follow-up study, researchers analyzed bone health decline and the effects of nusinersen in patients with spinal muscular atrophy (SMA) types 2 and 3. SMA is a progressive, ...

Singer Jesy Nelson has opened up sharing that her twin daughters have been diagnosed with Spinal Muscular Atrophy, but what ...